Rocket Pharma

### **Rocket Pharma: Revolutionizing Gene Therapy in Midtown Manhattan****Rocket Pharma**, located at 350 5th Avenue, Suite 7530, in the heart of Midtown Manhattan, is a cutting-edge pharmaceutical company dedicated to transforming the future of medicine through innovative gene therapy solutions.

With a mission to provide hope and healing for patients suffering from rare and devastating genetic diseases, Rocket Pharma has established itself as a leader in the biotechnology industry.

The company’s strategic location in New York City positions it at the crossroads of global innovation, research, and collaboration.#### **Pioneering Gene Therapy for Rare Diseases**Rocket Pharma specializes in developing gene therapies that address severe genetic disorders with limited or no existing treatment options.

By leveraging advanced scientific techniques such as adeno-associated virus (AAV) and lentiviral vector-based platforms, Rocket Pharma focuses on delivering one-time curative treatments.

Their pipeline includes therapies targeting conditions like Fanconi anemia (FA), Danon disease, Leukocyte Adhesion Deficiency-I (LAD-I), Pyruvate Kinase Deficiency (PKD), and Infantile Malignant Osteopetrosis (IMO).

These diseases often have life-threatening consequences, and Rocket Pharma’s groundbreaking work aims to improve patient outcomes significantly.#### **Commitment to Innovation and Collaboration**At its core, Rocket Pharma thrives on innovation.

The company collaborates with leading academic institutions, research organizations, and healthcare providers worldwide to accelerate the development of its therapies. By combining expertise in molecular biology, clinical research, and manufacturing processes, Rocket Pharma ensures that its treatments meet the highest standards of safety and efficacy.

This commitment to excellence has earned Rocket Pharma recognition as a trusted name in the field of gene therapy.#### **Patient-Centric Approach**Rocket Pharma places patients at the center of everything it does.

The company is deeply committed to addressing unmet medical needs by providing life-changing therapies that offer long-term benefits. Through rigorous clinical trials and transparent communication with patients and their families, Rocket Pharma fosters trust and confidence in its groundbreaking treatments.#### **Strategic Location in Midtown Manhattan**Situated within New York City’s iconic Empire State Building district, Rocket Pharma benefits from proximity to some of the world’s top medical institutions and biotech hubs.

This central location facilitates collaboration with key stakeholders while providing access to a diverse talent pool of scientists, researchers .spinner_b2T7 { animation: spinner_xe7Q .8s linear infinite } .spinner_YRVV { animation-delay: -.65s } .spinner_c9oY { animation-delay: -.5s } @keyframes spinner_xe7Q { 93.75%, 100% { r: 3px } 46.875% { r:.2px } }